The faculty members of the Department of Pediatrics at the University of Massachusetts Medical School teach medical students, interns and residents, and they conduct research in many topics related to child health such as HIV, leukemia, diabetes, cystic fibrosis, teen pregnancy, infant mortality, and health care delivery in the community. The University of Massachusetts Medical School is one of about 40 centers for the National Children’s Study (NCS), a federally funded longitudinal study to investigate the effects of the environment on the growth and development and health of children by following 100,000 children from pre-birth to age 21 years. Approximately 1000 of those children will be identified from Worcester County residents in Massachusetts. UMass is the only institution in Massachusetts to be identified as an NCS Center. This collection showcases the journal articles and other publications authored by faculty and researchers in the Department of Pediatrics.
To view this collection broken out by Department of Pediatrics divisions, visit Pediatric Divisions.
Publications from 2019
Condylomata acuminata (anogenital warts) contain accumulations of HIV-1 target cells that may provide portals for HIV transmission, Jeffrey Pudney, Zoon Wangu, Lori Panther, Dana Fugelso, Jai Marathe, Manish Sagar, Joseph A. Politch, and Deborah J. Anderson
How we approach: Severe congenital neutropenia and myelofibrosis due to mutations in VPS45, Bella Shadur, Nathalie Asherie, Peter E. Newburger, and Polina Stepensky
Publications from 2018
TIP55, a splice isoform of the KAT5 acetyltransferase, is essential for developmental gene regulation and organogenesis, Diwash Acharya, Bernadette Nera, Zachary J. Milstone, Lauren Bourke, Yeonsoo Yoon, Jaime A. Rivera-Pérez, Chinmay M. Trivedi, and Thomas G. Fazzio
Guidelines for sedation and anesthesia in GI endoscopy, ASGE Standards of Practice Committee, Dayna S. Early, Jenifer R. Lightdale, and John M. DeWitt
A Child With an Unusual Retained Oral Foreign Body, Timothy Baloda, Megan L. McBurnie, and Theodore Macnow
Recommendations on the Indications for RBC Transfusion for the Critically Ill Child Receiving Support From Extracorporeal Membrane Oxygenation, Ventricular Assist, and Renal Replacement Therapy Devices From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Melania M. Bembea, Ira M. Cheifetz, James D. Fortenberry, Timothy E. Bunchman, Stacey L. Valentine, Scot T. Bateman, and Marie E. Steiner
The Pediatric Critical Care Transfusion and Anemia Expertise Initiative Consensus Conference Methodology, Melania M. Bembea, Stacey L. Valentine, Scot T. Bateman, Lisa M. Wilson, Blair Anton, Nancy E. Harger, and Karen A. Robinson
Safe and effective superoxide dismutase 1 silencing using artificial microRNA in macaques, Florie Borel, Gwladys Gernoux, Huaming Sun, Rachel Stock, Meghan Blackwood, Robert H. Brown Jr., and Christian Mueller
Editing out five Serpina1 paralogs to create a mouse model of genetic emphysema, Florie Borel, Huaming Sun, Marina Zieger, Andrew Cox, Brynn Cardozo, Weiying Li, Gabriella Oliveira, Airiel Davis, Alisha Gruntman, Terence R. Flotte, Michael H. Brodsky, Andrew M. Hoffman, Mai K. Elmallah, and Christian Mueller
Lack of acute xenogeneic graft- versus-host disease, but retention of T-cell function following engraftment of human peripheral blood mononuclear cells in NSG mice deficient in MHC class I and II expression, Michael A. Brehm, Laurie L. Kenney, Michael V. Wiles, Benjamin E. Low, Roland M. Tisch, Lisa Burzenski, Christian Mueller, Dale L. Greiner, and Leonard D. Shultz
Expression of inflammatory markers in women with perinatal depressive symptoms, Rachel Buglione-Corbett, Kristina M. Deligiannidis, Katherine Leung, Ning Zhang, Mary M. Lee, Milagros C. Rosal, and Tiffany A. Moore Simas
Meeting the Late-Career Needs of Faculty Transitioning Through Retirement: One Institution's Approach, Joanna Cain, Marianne E. Felice, Judith K. Ockene, Robert J. Milner, John L. Congdon, Stephen Tosi, and Luanne A. Thorndyke
Trisomy silencing by XIST normalizes Down syndrome cell pathogenesis demonstrated for hematopoietic defects in vitro, Jen-Chieh Chiang, Jun Jiang, Peter E. Newburger, and Jeanne B. Lawrence
Assuring Integrity in the Residency Match Process, Sonia N. Chimienti, Deborah M. DeMarco, Terence R. Flotte, and Michael F. Collins
Recommendations on RBC Transfusion in Infants and Children With Acquired and Congenital Heart Disease From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Jill M. Cholette, Ariane Willems, Stacey L. Valentine, Scot T. Bateman, and Steven M. Schwartz
Small RNAs gained during epididymal transit of sperm are essential for embryonic development in mice, Colin C. Conine, Fengyun Sun, Lina Song, Jaime A. Rivera-Perez, and Oliver J. Rando
Small RNAs Gained during Epididymal Transit of Sperm Are Essential for Embryonic Development in Mice, Colin C. Conine, Fengyun Sun, Lina Song, Jaime A. Rivera-Perez, and Oliver J. Rando
Recommendations on RBC Transfusions in Critically Ill Children With Acute Respiratory Failure From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Pierre Demaret, Guillaume Emeriaud, Nabil E. Hassan, Martin C. J. Kneyber, Stacey L. Valentine, Scot T. Bateman, and Marisa Tucci
Recommendations on RBC Transfusion in General Critically Ill Children Based on Hemoglobin and/or Physiologic Thresholds From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Allan Doctor, Jill M. Cholette, Kenneth E. Remy, Andrew Argent, Jeffrey L. Carson, Stacey L. Valentine, Scot T. Bateman, and Jacques Lacroix
Airway Basal Cells Are the Key for Cystic Fibrosis Gene Therapy, Terence R. Flotte
Recombinant Adeno-Associated Virus-Based Gene Therapy for Disorders Detected by Newborn Screening: Inherent Limitations of This Approach, Terence R. Flotte
Severe Toxicity in Nonhuman Primates and Piglets with Systemic High-Dose Administration of Adeno-Associated Virus Serotype 9-Like Vectors: Putting Patients First, Terence R. Flotte and Hildegard Buning
Childhood Trauma Management in Primary Care, Heather Forkey and Anne-Marie Conn
Gene expression in chronic granulomatous disease and interferon-gamma receptor-deficient cells treated in vitro with interferon-gamma, Josias B. Frazao, Martino Colombo, Cedric Simillion, Adem Bilican, Irene Keller, Daniel Wuthrich, Zhiqing Zhu, Michal J. Okoniewski, Remy Bruggmann, Antonio Condino-Neto, and Peter E. Newburger
The clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study, Rachael F. Grace, Peter E. Newburger, and Wilma Barcellini
Endocrine disrupters and pubertal timing, Louise C. Greenspan and Mary M. Lee
Differences in self-reported weekend catch up sleep between children and adolescents with and without primary hypertension, Neena Gupta, Louise Maranda, and Rakesh Gupta
Self-Reported Management of IV Fluids and Fluid Accumulation in Children With Acute Respiratory Failure, Amanda B. Hassinger and Stacey L. Valentine
Inhibition of protein arginine methyltransferase 5 enhances hepatic mitochondrial biogenesis, Lei Huang, Jehnan Liu, Xiao-Ou Zhang, Katelyn Sibley, Sonia M. Najjar, Mary M. Lee, and Joae Qiong Wu
Recommendations on RBC Transfusion in Critically Ill Children With Nonlife-Threatening Bleeding or Hemorrhagic Shock From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Oliver Karam, Robert T. Russell, Paul Stricker, Adam M. Vogel, Scot T. Bateman, Stacey L. Valentine, and Philip C. Spinella
Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease, Allison M. Keeler, Marina Zieger, Sophia H. Todeasa, Angela L. McCall, Jennifer C. Gifford, Samantha Birsak, Sourav Roy Choudhury, Barry J. Byrne, Miguel Sena-Esteves, and Mai K. Elmallah
Single-Center Experience With Liver Transplant Using Donors With Very High Transaminase Levels, Paulo N.A. Martins, Amanda Rawson, Babak Movahedi, Isabel M. A. Bruggenwirth, Natasha H. Dolgin, Ann-Britt Martins, Paria Mahboub, and Adel Bozorgzadeh
Recommendations on RBC Transfusions for Critically Ill Children With Nonhemorrhagic Shock From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Jennifer A. Muszynski, Nina A. Guzzetta, Mark W. Hall, Duncan Macrae, Stacey L. Valentine, Scot T. Bateman, and Philip C. Spinella
"How I approach..."- A new series in Pediatric Blood and Cancer, Peter E. Newburger and Thomas G. Gross
Comment on Redondo et al. Racial/Ethnic Minority Youth With Recent-Onset Type 1 Diabetes Have Poor Prognostic Factors. Diabetes Care 2018;41:1017-1024, Benjamin U. Nwosu
Data from: Tobacco smoke exposure is an independent predictor of vitamin D deficiency in US children, Benjamin U. Nwosu and Philip Kum-Nji
Tobacco smoke exposure is an independent predictor of vitamin D deficiency in US children, Benjamin U. Nwosu and Philip Kum-Nji
Children with type 1 diabetes who experienced a honeymoon phase had significantly lower LDL cholesterol 5 years after diagnosis, Benjamin U. Nwosu, Bo Zhang, Sanaa S. Ayyoub, Stephanie Choi, Tony R. Villalobos-Ortiz, Laura C. Alonso, and Bruce A. Barton
Data from: Children with type 1 diabetes who experienced a honeymoon phase had significantly lower LDL cholesterol 5 years after diagnosis, Benjamin U. Nwosu, Bo Zhang, Sanaa S. Ayyoub, Stephanie Choi, Tony R. Villalobos-Ortiz, Laura C. Alonso, and Bruce A. Barton
Delayed Treatment Acceleration in Patients with Rheumatoid Arthritis Who Have Inadequate Response to Initial Tumor Necrosis Factor Inhibitors: Data from the Corrona Registry, Dimitrios A. Pappas, Robert A. Gerber, Heather J. Litman, David Gruben, Jamie Geier, Winnie D. Hua, Connie Chen, YouFu Li, Joel M. Kremer, John S. Andrews, and Jeffrey A. Bourret
Results at 5 Years After Gene Therapy for RPE65-Deficient Retinal Dystrophy, Mark E. Pennesi, Richard G. Weleber, Paul Yang, Chris Whitebirch, Beverly Thean, Terence R. Flotte, Margaret Humphries, Elvira Chegarnov, Kathleen N. Beasley, J. Timothy Stout, and Jeffrey D. Chulay
Aerobic Glycolysis Is Essential for Normal Rod Function and Controls Secondary Cone Death in Retinitis Pigmentosa, Lolita Petit, Shan Ma, Joris Cipi, Shun-Yun Cheng, Marina Zieger, Nissim Hay, and Claudio Punzo
Aerobic Glycolysis Is Essential for Normal Rod Function and Controls Secondary Cone Death in Retinitis Pigmentosa, Lolita Petit, Shan Ma, Joris Cipi, Shun-Yun Cheng, Marina Zieger, Nissim Hay, and Claudio Punzo
Peripubertal serum dioxin concentrations and subsequent sperm methylome profiles of young Russian adults, J. Richard Pilsner, Mary M. Lee, Evgeny Rogaev, and Oleg Sergeyev
The optimization of home oxygen weaning in premature infants trial: Design, rationale, methods, and lessons learned, Alexander Procaskey, Heather White, Tregony Simoneau, Nadav Traeger, Thomas Lahiri, Elie G. Abu Jawdeh, Ted M. Kremer, Catherine Sheils, Kathleen Meyer, Ted Rosenkrantz, Sankaran Krishnan, Tyler Hartman, Henry Feldman, and Lawrence M. Rhein
Clinical and economic burden of procedural sedation-related adverse events and their outcomes: analysis from five countries, Rhodri Saunders, Jason A. Davis, Peter Kranke, Rachel Weissbrod, David K. Whitaker, and Jenifer R. Lightdale
Vomiting in Children, T. Matthew Shields and Jenifer R. Lightdale
Prevalence and characteristics of sleep-disordered breathing in familial dysautonomia, Kanwaljit Singh, Jose-Alberto Palma, Horacio Kaufmann, Nataliya Tkachenko, Lucy Norcliffe-Kaufmann, Christy Spalink, Mikhail Kazachkov, and Sanjeev V. Kothare
CHD3 helicase domain mutations cause a neurodevelopmental syndrome with macrocephaly and impaired speech and language, Lot Snijders Blok, Inderneel Sahai, and Philippe M. Campeau
In vivo genome editing partially restores alpha1-antitrypsin in a murine model of AAT deficiency, Chun-Qing Song, Dan Wang, Tingting Jiang, Kevin O'Connor, Qiushi Tang, Lingling Cai, Xiangrui Li, Zhiping Weng, Hao Yin, Guangping Gao, Christian Mueller, Terence R. Flotte, and Wen Xue
Case Definitions for Conditions Identified by Newborn Screening Public Health Surveillance, Marci K. Sontag, Deboshree Sarkar, Anne Marie Comeau, Kathryn Hassell, Lorenzo D. Botto, Richard Parad, Susan R. Rose, Kupper A. Wintergerst, Kim Smith-Whitley, Sikha Singh, Careema Yusuf, Jelili Ojodu, Sara Copeland, and Cynthia F. Hinton
Implementation of the Recommendations for RBC Transfusions for Critically Ill Children From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Katherine M. Steffen, Scot T. Bateman, Stacey L. Valentine, Sara Small, Philip C. Spinella, and Allan Doctor
Recommendations on RBC Transfusion Support in Children With Hematologic and Oncologic Diagnoses From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Marie E. Steiner, Nicole D. Zantek, Simon J. Stanworth, Robert I. Parker, Stacey L. Valentine, Leslie E. Lehmann, Cassandra D. Josephson, Scot T. Bateman, and Naomi L. C. Luban
Serum anti-flagellin and anti-lipopolysaccharide immunoglobulins as predictors of linear growth faltering in Pakistani infants at risk for environmental enteric dysfunction, Sana Syed, Najeeha T. Iqbal, Kamran Sadiq, Jennie Z. Ma, Tauseef Akhund, Wenjun Xin, Sean R. Moore, Enju Liu, Shahida Qureshi, Kerri B. Gosselin, Andrew Gewirtz, Christopher P. Duggan, and S Asad. Ali
Consensus Recommendations for RBC Transfusion Practice in Critically Ill Children From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Stacey L. Valentine and Scot T. Bateman
Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study, Eduard J. van Beers, Peter E. Newburger, and Rachael F. Grace
A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in Neonates, Dan Wang, Shaoyong Li, Dominic J. Gessler, Jun Xie, Li Zhong, Jia Li, Karen Tran, Kim Van Vliet, Lingzhi Ren, Qin Su, Ran He, Jason E. Goetzmann, Terence R. Flotte, Mavis Agbandje-McKenna, and Guangping Gao
Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer, Dan Wang, Li Zhong, Mengxin Li, Jia Li, Karen Tran, Lingzhi Ren, Ran He, Jun Xie, Richard P. Moser, Cara Fraser, Tim Kuchel, Miguel Sena-Esteves, Terence R. Flotte, Neil Aronin, and Guangping Gao
Similarity of chest X-ray and thermal imaging of focal pneumonia: a randomised proof of concept study at a large urban teaching hospital, Linda T. Wang, Robert H. Cleveland, William Binder, Robert G. Zwerdling, Caterina Stamoulis, Thomas Ptak, Mindy Sherman, Kenan Haver, Pallavi Sagar, and Patricia Hibberd
ARMMs as a versatile platform for intracellular delivery of macromolecules, Qiyu Wang, Jiujiu Yu, Tatenda Kadungure, Joseph Beyene, Hong Zhang, and Quan Lu
Evaluating Patient-Centered Outcomes in Clinical Trials of Procedural Sedation, Part 2 Safety: Sedation Consortium on Endpoints and Procedures for Treatment, Education, and Research Recommendations, Denham S. Ward and Jenifer R. Lightdale
Streamlined ex vivo and in vivo genome editing in mouse embryos using recombinant adeno-associated viruses, Yeonsoo Yoon, Dan Wang, Phillip W. L. Tai, Joy Riley, Guangping Gao, and Jaime A. Rivera-Perez
Nuclear organization mediates cancer-compromised genetic and epigenetic control, Sayyed K. Zaidi, Andrew J. Fritz, Kirsten M. Tracy, Jonathan A. Gordon, Coralee E. Tye, Joseph Boyd, Andre J. Van Wijnen, Jeffrey A. Nickerson, Anthony N. Imbalzano, Jane B. Lian, Janet L. Stein, and Gary S. Stein
Recommendations on Selection and Processing of RBC Components for Pediatric Patients From the Pediatric Critical Care Transfusion and Anemia Expertise Initiative, Nicole D. Zantek, Robert I. Parker, Leo M. van de Watering, Cassandra D. Josephson, Scot T. Bateman, Stacey L. Valentine, and Meghan Delaney
Publications from 2017
KAT-Independent Gene Regulation by Tip60 Promotes ESC Self-Renewal but Not Pluripotency, Diwash Acharya, Sarah J. Hainer, Yeonsoo Yoon, Feng Wang, Ingolf Bach, Jaime A. Rivera-Perez, and Thomas G. Fazzio
Long-Acting Reversible Contraception: An Essential Guide for Pediatric Primary Care Providers, Suzanne Allen and Erin Barlow
Pediatric Poisonings: Do They Really Need That PICU Bed, Scot T. Bateman
It is Time for Zero Tolerance for Sexual Harassment in Academic Medicine, Carol K. Bates, Reshma Jagsi, Lynn K. Gordon, Elizabeth Travis, Archana Chatterjee, Marin Gillis, Olivia Means, Linda Chaudron, Rebecca Ganetzky, Martha Gulati, Barbara Fivush, Poonam Sharma, Amelia Grover, Diana Lautenberger, and Terence R. Flotte
A Circulating microRNA Signature Predicts Age-Based Development of Lymphoma, Afshin Beheshti, Charles Vanderburg, J. Tyson McDonald, Charusheila Ramkumar, Tatenda Kadungure, Hong Zhang, Ronald B. Gartenhaus, and Andrew M. Evens
Human Papillomavirus Vaccine Update, Diane R. Blake and Amy B. Middleman
Wide Variation Found in Care of Opioid-Exposed Newborns, Debra L. Bogen, Bonny L. Whalen, Laura R. Kair, Mark Vining, and Beth A. King
Design, Cloning, and In Vitro Screening of Artificial miRNAs to Silence Alpha-1 Antitrypsin, Florie Borel and Christian Mueller
Survival Advantage of Both Human Hepatocyte Xenografts and Genome-Edited Hepatocytes for Treatment of alpha-1 Antitrypsin Deficiency, Florie Borel, Qiushi Tang, Gwladys Gernoux, Cynthia Greer, Ziqiong Wang, Adi Barzel, Mark A. Kay, Leonard D. Shultz, Dale L. Greiner, Terence R. Flotte, Michael A. Brehm, and Christian Mueller
Quantification of Z-AAT by a Z-Specific "Sandwich" ELISA, Florie Borel, Qiushi Tang, and Christian Mueller
Intervention Fidelity: Monitoring Drift, Providing Feedback, and Assessing the Control Condition, Carol A. Bova, Carol A. Jaffarian, Sybil L. Crawford, Jose Bernardo Quintos, Mary M. Lee, and Susan Sullivan-Bolyai
Peripubertal blood lead levels and growth among Russian boys, Jane S. Burns, Paige L. Williams, Mary M. Lee, Boris Revich, Oleg Sergeyev, Russ Hauser, and Susan A. Korrick
Class I-restricted T-cell responses to a polymorphic peptide in a gene therapy clinical trial for alpha-1-antitrypsin deficiency, Roberto Calcedo, Suryanarayan Somanathan, Qiuyue Qin, Michael R. Betts, Andrew J. Rech, Robert H. Vonderheide, Christian Mueller, Terence R. Flotte, and James M. Wilson
Adverse events associated with ERCP, Vinay Chandrasekhara, Jenifer R. Lightdale, and John M. DeWitt
New Assessments and Treatments in ASD, Roula N. Choueiri and Andrew W. Zimmerman
Quantification of Murine AAT by Direct ELISA, Andrew Cox and Christian Mueller
An Unusual Manifestation of Celiac Disease in an Adolescent With Down Syndrome and Graves Disease, Ana L. Creo, Ninfa Candela, Mary M. Lee, and Penny M. Feldman
Long-Term Effects of G-CSF Therapy in Cyclic Neutropenia, David C. Dale, AudreyAnna Bolyard, Tracy Marrero, Vahagn Makaryan, MaryAnn Bonilla, Daniel C. Link, Peter E. Newburger, Akiko Shimamura, Laurence A. Boxer, and Charles Spiekerman
Gene Therapy with an Adeno-Associated Viral Vector Expressing Human Interleukin-2 Alters Immune System Homeostasis in Humanized Mice, Philip A. Durost, Ken-Edwin Aryee, Fatima Manzoor, Roland M. Tisch, Christian Mueller, Agata Jurczyk, Leonard D. Shultz, and Michael A. Brehm
Pediatric Obstructive Sleep Apnea in High-Risk Populations: Clinical Implications, Mai K. Elmallah, Evan Bailey, Michelle Trivedi, Ted M. Kremer, and Lawrence M. Rhein
A C9ORF72 BAC mouse model recapitulates key epigenetic perturbations of ALS/FTD, Rustam Esanov, Gabriela Toro Cabrera, Nadja S. Andrade, Tania F. Gendron, Robert H. Brown Jr., Michael Benatar, Claes Wahlestedt, Christian Mueller, and Zane Zeier
An oral HemokineTM, alpha-methylhydrocinnamate, enhances myeloid and neutrophil recovery following irradiation in vivo, Douglas V. Faller, Serguei A. Castaneda, Daohong Zhou, Merriline Vedamony, Peter E. Newburger, Gary L. White, Stanley Kosanke, P. Artur Plett, Christie M. Orschell, Michael S. Boosalis, and Susan P. Perrine
The role of endoscopy in subepithelial lesions of the GI tract, Ashley L. Faulx, Shivangi Kothari, Ruben D. Acosta, Deepak Agrawal, David H. Bruining, Vinay Chandrasekhara, Mohamad A. Eloubeidi, Robert D. Fanelli, Suryakanth R. Gurudu, Mouen A. Khashab, Jenifer R. Lightdale, V. Raman Muthusamy, Aasma Shaukat, Bashar J. Qumseya, Amy Wang, Sachin B. Wani, Julie Yang, and John M. DeWitt
Guidelines for privileging, credentialing, and proctoring to perform GI endoscopy, Ashley L. Faulx, Jenifer R. Lightdale, and John M. DeWitt
A Primer for Primary Care Clinicians Caring for Sexually Active Adolescents, Marianne E. Felice
Adeno-Associated Virus-Human Bocavirus 1 Chimeric Vectors: Ferreting Out Their Role in Airway Gene Therapy, Terence R. Flotte
Empty Adeno-Associated Virus Capsids: Contaminant or Natural Decoy, Terence R. Flotte
European Society of Gene and Cell Therapy (ESGCT) at 25: A Gene Therapy Community at Its Prime and on the Move, Terence R. Flotte
Gene Therapy for Alcoholism and Other Substance Use Disorders, Terence R. Flotte
One More Controversy: Adeno-Associated Virus in Stem Cells, Terence R. Flotte
Sleeping Beauty Awakens New Interest, Terence R. Flotte
The Negative Effects of Immigration Restrictions on the Gene Therapy Community, Terence R. Flotte
Therapeutic Advances in Germany and Beyond, Terence R. Flotte
The Science Policy Implications of a Trump Presidency, Terence R. Flotte
The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute, Terence R. Flotte, Eric Daniels, Janet Benson, Jenee M. Bevett-Rose, Kenneth Cornetta, Margaret Diggins, Julie Johnston, Susan Sepelak, Johannes C. M. van der Loo, James M. Wilson, and Cheryl L. McDonald
AAV Is Now a Medicine: We Had Better Get This Right, Terence R. Flotte and Guangping Gao